The Medicines Of Tomorrow: A Primer On The Gene Editing Landscape

By Adrian Oliver, Ph.D., Senior Scientist of Technology Development, Life Edit Therapeutics

CRISPR gene editing offers the potential to permanently treat genetic diseases with just a single dose of medicine. This concept of “one and done” has revolutionized not only how we think about treating disease; it has also revolutionized how therapies for many diseases are now being discovered and developed.

While many people understand the potential of CRISPR technology to treat genetic diseases with previously unmet medical needs – it targets the mutated segment of DNA within the disease-related gene to “correct” it – many are still keen to understand how this novel technology works, which diseases it can and cannot treat, and the future opportunities enabled by this modality.

Learn more about the distinction between gene therapy and gene editing as well as the therapeutic potential of CRISPR treatments and the challenges that remain on the path toward clinical trials and eventual commercialization.